Institution

Scientific Institute San Raffael

Biography

She has published > 60 papers in international scientific journals (Total Impact Factor 585.347). Overall, her papers have been cited more than 8477 times (Scopus h-index: 40).
Her fields of interest and research are hematopoietic stem cell biology, transcriptional regulation, engineering of viral vectors, development of preclinical models for gene therapy, gene therapy for beta-thalassemia. She is an internationally recognized expert on gene therapy for hematopoietic diseases and she is the project leader of the clinical trial of gene therapy for beta-thalassemia TIGET BTHAL (NCT02453477).